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Niemann-Pick type C disease (NPC)

A rare genetic disease

NPC disease is a rare genetic disease inherited in a recessive pattern. This means that both parents carry the altered gene despite not showing any sign of the disease.

NPCThis alteration induces the lack of function in a protein necessary to transport cholesterol around the cell. When cholesterol cannot be transported, it builds up inside the cell and causes a general malfunction, leading to the signs of the disease that you can see in your family member.

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